Real-Life Outcome After Gene Replacement Therapy for Spinal Muscular Atrophy: A Multicenter Experience
Article in Pediatric Neurology (April 2023)
The most recent citing publications are shown below. View all 6 publications that cite this research output on Dimensions.
Article in Pediatric Neurology (April 2023)
Article in Gene Therapy (October 2021)
Article in BioDrugs (June 2021)