.#openaccess : Appraisal of patient-reported outcome measures in analogous diseases and recommendations for use in phase II and III clinical trials of pyruvate kinase deficiency, in new Quality of Life Research @ISOQOL #QoL #QLR #PROMs https://t.co/jLcSBIH
RT @jrboehnke: What to do if there is no patient-reported outcome measure for a target condition? Learning from & about instruments that ar…
What to do if there is no patient-reported outcome measure for a target condition? Learning from & about instruments that are available for analogue conditions may help: https://t.co/2Tnqffmstp #openaccess #PRO #rarediseases #QoL #QLR #HRQoL