ENZYMATIC REPLACEMENT THERAPY AND ANTISENSE THERAPY FOR POMPE DISEASE Application WO-2018231060-A1 World Intellectual Property Organisation (WIPO) 20 Dec 2018
NATURAL CRYPTIC EXON REMOVAL BY PAIRS OF ANTISENSE OLIGONUCLEOTIDES Application WO-2018026284-A1 World Intellectual Property Organisation (WIPO) 08 Feb 2018