Modified U6 promoter system for tissue specific expression Grant US-11939579-B2 United States of America 26 Mar 2024
Compositions and methods for transient delivery of nucleases Grant US-11920168-B2 United States of America 05 Mar 2024
Recombinant adeno-associated viruses for delivering gene editing molecules to embryonic… Grant US-11882815-B2 United States of America 30 Jan 2024
Methods of treating amyotrophic lateral sclerosis (ALS) Grant US-11859179-B2 United States of America 02 Jan 2024
Anti-angiogenic miRNA therapeutics for inhibiting corneal neovascularization Grant US-11851657-B2 United States of America 26 Dec 2023
Method to enhance the efficiency of systemic AAV gene delivery to the central nervous… Grant US-11826433-B2 United States of America 28 Nov 2023
Compositions and methods for modulating dysferlin expression Grant US-11827886-B2 United States of America 28 Nov 2023
Recombinant virus products and methods for inhibition of expression of DUX4 Grant US-11802291-B2 United States of America 31 Oct 2023
RAAV-based compositions and methods for treating amyotrophic lateral sclerosis Grant US-11760999-B2 United States of America 19 Sep 2023
SOD1 dual expression vectors and uses thereof Grant US-11739330-B2 United States of America 29 Aug 2023
Compositions and methods for treatment of cardiac diseases Grant US-11566243-B2 United States of America 31 Jan 2023
Prostate-targeting adeno-associated virus serotype vectors Grant US-11426469-B2 United States of America 30 Aug 2022
AAV-based treatment of cholesterol-related disorders Grant US-11421230-B2 United States of America 23 Aug 2022
Compositions and methods for treatment of cardiac diseases Grant US-11421232-B2 United States of America 23 Aug 2022
Methods and compositions for treating metabolic imbalance Grant US-11413356-B2 United States of America 16 Aug 2022
Modified U6 promoter system for tissue specific expression Grant US-11345913-B2 United States of America 31 May 2022
MIR-375- AND MIR-1-REGULATED COXSACKIEVIRUS B3 HAS NO PANCREAS AND HEART TOXICITY BUT… Application WO-2022100898-A1 World Intellectual Property Organisation (WIPO) 19 May 2022
Methods and compositions for treating metabolic imbalance in neurodegenerative disease Grant US-11253576-B2 United States of America 22 Feb 2022
Compositions and methods for selective inhibition of grainyhead-like protein expression Grant US-11207426-B2 United States of America 28 Dec 2021
Compositions and methods for treatment of cardiac diseases Grant US-11124793-B2 United States of America 21 Sep 2021
Recombinant virus products and methods for inhibition of expression of myotilin Grant US-11091760-B2 United States of America 17 Aug 2021
Anti-angiogenic miRNA therapeutics for inhibiting corneal neovascularization Grant US-11060088-B2 United States of America 13 Jul 2021
Heterologous targeting peptide grafted AAVS Grant US-11014976-B2 United States of America 25 May 2021
Recombinant AAV vectors useful for reducing immunity against transgene products Grant US-10975391-B2 United States of America 13 Apr 2021
RAAV-based compositions and methods for treating amyotrophic lateral sclerosis Grant US-10954518-B2 United States of America 23 Mar 2021
Recombinant AAVS having useful transcytosis properties Grant US-10894949-B2 United States of America 19 Jan 2021
RAAV-based compositions and methods for treating amyotrophic lateral sclerosis Grant US-10851375-B2 United States of America 01 Dec 2020
CNS targeting AAV vectors and methods of use thereof Grant US-10731178-B2 United States of America 04 Aug 2020
AAV-based treatment of cholesterol-related disorders Grant US-10731158-B2 United States of America 04 Aug 2020
RAAV-based compositions and methods for treating amyotrophic lateral sclerosis Grant US-10711274-B2 United States of America 14 Jul 2020
High efficiency library-identified AAV vectors Grant US-10711270-B2 United States of America 14 Jul 2020
Compositions and methods for modulating dysferlin expression Grant US-10689653-B2 United States of America 23 Jun 2020
Compositions and methods for transient delivery of nucleases Grant US-10584321-B2 United States of America 10 Mar 2020
Heterologous targeting peptide grafted AAVS Grant US-10370432-B2 United States of America 06 Aug 2019
Recombinant virus products and methods for inhibition of expression of DUX4 Grant US-10301649-B2 United States of America 28 May 2019
RAAV-based compositions and methods for treating amyotrophic lateral sclerosis Grant US-10280418-B2 United States of America 07 May 2019
AAV-based treatment of cholesterol-related disorders Grant US-10202600-B2 United States of America 12 Feb 2019
Recombinant virus products and methods for inhibition of expression of myotilin Grant US-10196636-B2 United States of America 05 Feb 2019
MULTICISTRONIC EXPRESSION CONSTRUCTS Application US-20170145439-A1 United States of America 25 May 2017
Recombinant virus products and methods for inhibition of expression of DUX4 Grant US-9469851-B2 United States of America 18 Oct 2016
Recombinant virus products and methods for inhibition of expression of myotilin Grant US-9133482-B2 United States of America 15 Sep 2015