Methods and compositions for delivery of viral vectors across the blood-brain barrier Grant US-11905533-B2 United States of America 20 Feb 2024
Receptors for ligand-dependent transcriptional regulation Grant US-11897932-B2 United States of America 13 Feb 2024
NUCLEIC ACID ANTISENSE OLIGOMER READTHROUGH OF NONSENSE CODONS Application WO-2024025824-A2 World Intellectual Property Organisation (WIPO) 01 Feb 2024
Synthetic immunomodulation with a CRISPR super-repressor in vivo Grant US-11884925-B2 United States of America 30 Jan 2024
Method for the treatment of mucopolysaccharidosis type I Grant US-11857641-B2 United States of America 02 Jan 2024
HIGH FIDELITY NUCLEOTIDE POLYMERASE CHIMERIC PRIME EDITOR SYSTEMS Application WO-2023235501-A1 World Intellectual Property Organisation (WIPO) 07 Dec 2023
FUSION PROTEIN AND USE FOR BIOVCONVERTING MOLECULES Application WO-2023233094-A1 World Intellectual Property Organisation (WIPO) 07 Dec 2023
COMPOSITIONS AND METHODS FOR TREATING HER2 POSITIVE METASTATIC BREAST CANCER AND OTHER… Application WO-2023196893-A1 World Intellectual Property Organisation (WIPO) 12 Oct 2023
AAV-ABCD1 constructs and use for treatment or prevention of adrenoleukodystrophy (ALD) and… Grant US-11779655-B2 United States of America 10 Oct 2023
Gene therapy vectors for treating heart disease Grant US-11759531-B2 United States of America 19 Sep 2023
COMPOSITIONS AND METHODS FOR EFFICIENT AND STABLE GENETIC MODIFICATION OF EUKARYOTIC CELLS Application WO-2023173137-A1 World Intellectual Property Organisation (WIPO) 14 Sep 2023
USE OF CIRCUTRN IN PREPARATION OF DRUG FOR TREATING HEART FAILURE, RECOMBINANT VECTOR… Application US-20230272417-A1 United States of America 31 Aug 2023
Delivery of card protein as therapy for ocular inflammation Grant US-11739130-B2 United States of America 29 Aug 2023
Adeno-associated virus vector delivery of micro-dystrophin to treat muscular dystrophy Grant US-11723986-B2 United States of America 15 Aug 2023
Use of AAV-expressed M013 protein as an anti-inflammatory therapeutic Grant US-11685767-B2 United States of America 27 Jun 2023
RECOMBINANT AAV-CRUMBS HOMOLOGUE COMPOSITION AND METHODS FOR TREATING LCA-8 AND… Grant EP-3030665-B1 European Patent Office 07 Jun 2023
ISOLATED MODIFIED AAV9 CAPSID PROTEIN VP1 Application WO-2023022634-A1 World Intellectual Property Organisation (WIPO) 23 Feb 2023
ISOLATED MODIFIED AAV5 CAPSID PROTEIN VP1 Application WO-2023022633-A1 World Intellectual Property Organisation (WIPO) 23 Feb 2023
MODULAR PRIME EDITOR SYSTEMS FOR GENOME ENGINEERING Application WO-2023283246-A1 World Intellectual Property Organisation (WIPO) 12 Jan 2023
SYNERGISTIC COMBINATION OF RDCFV2 AND RDCVF2L FOR THE TREATMENT OF TAUOPATHIES Application WO-2023280926-A1 World Intellectual Property Organisation (WIPO) 12 Jan 2023
Adeno-associated virus vector delivery of muscle specific micro-dystrophin to treat… Grant US-11534501-B2 United States of America 27 Dec 2022
MACULAR TELANGIECTASIA TYPE 2 TREATMENT Application WO-2022251923-A1 World Intellectual Property Organisation (WIPO) 08 Dec 2022
Small angiotensin peptide expression system in mammalian cells Grant US-11512326-B2 United States of America 29 Nov 2022
PROTEIN HAVING HDGF (HEPATOMA-DERIVED GROWTH FACTOR) FUNCTION FOR USE IN TREATING AND… Application WO-2022195042-A1 World Intellectual Property Organisation (WIPO) 22 Sep 2022
Anellovirus compositions and methods of use Grant US-11446344-B1 United States of America 20 Sep 2022
Gene therapy vectors for treating heart disease Grant US-11446397-B2 United States of America 20 Sep 2022
Adeno-associated virus vector delivery of microRNA-29 and micro-dystrophin to treat… Grant US-11406717-B2 United States of America 09 Aug 2022
METHOD FOR PRODUCING AAV GENE DRUGS ON BASIS OF INDUCIBLE INSECT CELLS Application WO-2022160512-A1 World Intellectual Property Organisation (WIPO) 04 Aug 2022
AAV-ABCD1 CONSTRUCTS AND USE FOR TREATMENT OR PREVENTION OF ADRENOLEUKODYSTROPHY (ALD) AND… Application US-20220175965-A1 United States of America 09 Jun 2022
USE OF AMINOQUINOLINE COMPOUNDS FOR HIGHER GENE INTEGRATION Application WO-2022112596-A1 World Intellectual Property Organisation (WIPO) 02 Jun 2022
MODIFIED VIRAL PARTICLES FOR GENE THERAPY Application WO-2022101363-A1 World Intellectual Property Organisation (WIPO) 19 May 2022
VIRAL VECTORS AND NUCLEIC ACIDS FOR USE IN THE TREATMENT OF ILD, PF-ILD AND IPF Application WO-2022096092-A1 World Intellectual Property Organisation (WIPO) 12 May 2022
VIRAL VECTORS AND NUCLEIC ACIDS FOR USE IN THE TREATMENT OF ILD, PF-ILD AND IPF Application WO-2022096612-A2 World Intellectual Property Organisation (WIPO) 12 May 2022
VIRAL VECTORS AND NUCLEIC ACIDS FOR USE IN THE TREATMENT OF ILD, PF-ILD AND IPF Application WO-2022096563-A1 World Intellectual Property Organisation (WIPO) 12 May 2022
Adeno-associated virus vector delivery of microrna-29 to treat muscular dystrophy Grant US-11298429-B2 United States of America 12 Apr 2022
Methods for Treating Oculopharyngeal Muscular Dystrophy (OPMD) Application US-20220106594-A1 United States of America 07 Apr 2022
COMPOSITIONS AND METHODS FOR INHIBITING ALPHA-SYNUCLEIN AGGREGATION Application WO-2022066911-A1 World Intellectual Property Organisation (WIPO) 31 Mar 2022
Recombinant AAV-crumbs homologue composition and methods for treating LCA-8 and… Grant US-11246947-B2 United States of America 15 Feb 2022
Methods and materials for increasing viral vector infectivity Grant US-11207424-B2 United States of America 28 Dec 2021
VIRUS VECTORS FOR TARGETING OPHTHALMIC TISSUES Application US-20210371469-A1 United States of America 02 Dec 2021
FORMULATIONS FOR VIRAL VECTORS Application WO-2021243264-A2 World Intellectual Property Organisation (WIPO) 02 Dec 2021
COMPOUNDS BINDING TENASCIN-C (TNC) FOR USE IN THE TREATMENT OF DISEASES Application WO-2021233766-A1 World Intellectual Property Organisation (WIPO) 25 Nov 2021
COMPOUNDS BINDING TENASCIN-C (TNC) FOR USE IN THE TREATMENT OF DISEASES Application EP-3912994-A1 European Patent Office 24 Nov 2021
NUCLEIC ACIDS ENCODING HUMAN FUS PROTEIN AND USE IN THE TREATMENT OF AMYOTROPHIC LATERAL… Application WO-2021205010-A1 World Intellectual Property Organisation (WIPO) 14 Oct 2021
NUCLEIC ACIDS ENCODING HUMAN FUS PROTEIN AND USE IN THE TREATMENT OF AMYOTROPHIC LATERAL… Application EP-3892283-A1 European Patent Office 13 Oct 2021
Gene therapy vectors for treating heart disease Grant US-11129908-B2 United States of America 28 Sep 2021
PROGRAMMABLE SHELLS FOR VIRUS ENCAPSULATION Application WO-2021165528-A1 World Intellectual Property Organisation (WIPO) 26 Aug 2021
PROGRAMMABLE SHELLS FOR VIRUS ENCAPSULATION Application EP-3868893-A1 European Patent Office 25 Aug 2021
Delivery of Nrf2 as therapy for protection against reactive oxygen species Grant US-11053291-B2 United States of America 06 Jul 2021
TRANSGENE CASSETTES, AAV VECTORS AND AAV VIRAL VECTORS FOR THE EXPRESSION OF HUMAN CODON-OP… Application US-20210139934-A1 United States of America 13 May 2021
Recombinantly-modified adeno-associated virus helper vectors and their use to improve the… Grant US-11001859-B2 United States of America 11 May 2021
COMPOSITIONS AND METHODS FOR PRODUCING ADENO-ASSOCIATED VIRAL VECTORS Application WO-2021041375-A1 World Intellectual Property Organisation (WIPO) 04 Mar 2021
DRUG STABILIZED THERAPEUTIC TRANSGENES DELIVERED BY ADENO-ASSOCIATED VIRUS EXPRESSION Application US-20210046193-A1 United States of America 18 Feb 2021
TRIPARTITE SYSTEMS FOR PROTEIN DIMERIZATION AND METHODS OF USE Application WO-2021009692-A1 World Intellectual Property Organisation (WIPO) 21 Jan 2021
Compositions and methods for nucleic acid transfer Grant US-10894960-B2 United States of America 19 Jan 2021
VIRAL VECTORS AND NUCLEIC ACIDS FOR USE IN THE TREATMENT OF PF-ILD AND IPF Application WO-2020221911-A1 World Intellectual Property Organisation (WIPO) 05 Nov 2020
METHODS AND COMPOSITIONS FOR DELIVERY OF VIRAL VECTORS ACROSS THE BLOOD-BRAIN BARRIER Application US-20200325456-A1 United States of America 15 Oct 2020
HTRA1 MODULATION FOR TREATMENT OF AMD Application WO-2020210724-A1 World Intellectual Property Organisation (WIPO) 15 Oct 2020
Use of ion concentrations to increase the packaging efficiency of recombinant adeno-associa… Grant US-10801042-B1 United States of America 13 Oct 2020
COMPLEMENT FACTOR I AND COMPLEMENT FACTOR I COFACTOR, VECTORS ENCODING THEREFOR AND… Application WO-2020128535-A1 World Intellectual Property Organisation (WIPO) 25 Jun 2020
Recombinantly-modified adeno-associated virus (rAAV) having improved packaging efficiency Grant US-10653731-B1 United States of America 19 May 2020
METHODS FOR TREATING OCULOPHARYNGEAL MUSCULAR DYSTROPHY (OPMD) Application WO-2020077412-A1 World Intellectual Property Organisation (WIPO) 23 Apr 2020
METHOD FOR THE TREATMENT OF MUCOPOLYSACCHARIDOSIS TYPE II Application US-20200063160-A1 United States of America 27 Feb 2020
Recombinantly-modified adeno-associated virus helper vectors and their use to improve the… Grant US-10557149-B1 United States of America 11 Feb 2020
FULLY-HUMAN POST-TRANSLATIONALLY MODIFIED ANTIBODY THERAPEUTICS Application WO-2019079496-A3 World Intellectual Property Organisation (WIPO) 13 Jun 2019
RECOMBINANT AAV-CRUMBS HOMOLOGUE COMPOSITION AND METHODS FOR TREATING LCA-8 AND… Application EP-3030665-A1 European Patent Office 15 Jun 2016