DMD example: exon skipping slows down disease progression (at best) rather than improving function. Is this something patients want? @ParentProjectMD & Holly Peay did a preference study showing patients/caregivers do want this at each disease stage htt
RT @oligogirl: This study https://t.co/SCdt5MQd1e confirms this. Also talking to patients taught me that they mostly want to postpone losin…
RT @oligogirl: This study https://t.co/SCdt5MQd1e confirms this. Also talking to patients taught me that they mostly want to postpone losin…
RT @oligogirl: This study https://t.co/SCdt5MQd1e confirms this. Also talking to patients taught me that they mostly want to postpone losin…
RT @oligogirl: This study https://t.co/SCdt5MQd1e confirms this. Also talking to patients taught me that they mostly want to postpone losin…
This study https://t.co/SCdt5MQd1e confirms this. Also talking to patients taught me that they mostly want to postpone losing next function https://t.co/QtRrZCXrDy